• National Survey Seeks to Assess Full Social, Economic Burdens of Rare Diseases in US
  • CHMP Favors At-home Injection Form of Remsima for Europe
  • Alexion Charitable Foundation Giving $1.1M to Assist Rare Disease Community During Pandemic
  • Simponi Effective, Including in Patients Who Tried Other TNF Blockers, Data Show
  • Cosentyx Approved in US to Treat Active nr-axSpA
  • Nepexto, Enbrel Biosimilar, Approved to Treat Patients in Europe
  • Coalition Will Address Racial Disparities in Rare Disease Communities
  • FDA Approves Taltz for Non-radiographic Axial Spondyloarthritis
  • UK Study Evaluating COVID-19 Lockdown Effect on Musculoskeletal Health
  • COVID-19 Delaying Rare Disease and Gene Therapy Trials, Pharma Execs Say
  • Eurordis Urges Expansion of Newborn Screening Initiatives Across Europe
  • Unity and EU-wide Efforts Focus of Online Rare Disease Meeting